Doctors in the UK are claiming to have performed a monumental medical breakthrough. Using a form of gene therapy, they successfully treated—for the first time—the neurodegenerative disorder Huntington’s disease.

On Wednesday, the company uniQure announced the results of its phase I/II trial testing the therapy, code-named AMT-130. The trial, conducted with the help of researchers from University College London, found that AMT-130 slowed the progression of people’s symptoms by 75%. It also appeared to reduce the death of brain cells, a signature feature of the disease. It’s still early days, but the results could soon herald the arrival of a remarkable treatment for the currently life-shortening condition.

“I believe these groundbreaking data are the most convincing in the field to date

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