WHITE OAK, MD - JULY 20: A sign for the Food And Drug Administration is seen outside of the headquarters on July 20, 2020 in White Oak, Maryland. (Photo by Sarah Silbiger/Getty Images) Getty Images

Millions of people worldwide live with mitochondrial diseases. These are inherited conditions that make it hard for the body’s cells to produce energy. For a long time, patients had few options besides treatments that helped with symptoms. Now, a new drug has been approved that treats the root cause of some mitochondrial diseases. This breakthrough gives hope to many families and sets a new direction for future treatments.

What Is Mitochondrial Disease?

Mitochondrial diseases occur when a person’s genes cause problems in the mitochondria, our cells’ power plants. When they can’t do th

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