TAMPA, Fla. (WFLA) — For the first time, scientists have successfully treated someone suffering from Huntington's disease, a fatal genetic illness with no cure.
The Mayo Clinic reports that the condition causes nerve cells in the brain to decay over a period of time, causing a decline in motion, cognitive abilities and mental health. It typically manifests when someone enters their 30s or 40s, but it can also begin in patients under 20 years of age, who are diagnosed with juvenile Huntington's disease.
According to a press release, gene therapy company uniQure announced positive results from a study of a gene therapy known as AMT-130.
The therapy works through a neurosurgical procedure that infuses AMT-130 three times on each side of the brain.
The gene therapy then uses a non-disease